FIREFISH Parts 1 and 2: 24-month Safety and Efficacy of Risdiplam in Type 1 SMA

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dc.contributorSistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSP
dc.contributor.authorDARRAS, Basil T.
dc.contributor.authorBOESPFLUG-TANGUY, Odile
dc.contributor.authorDAY, John W.
dc.contributor.authorDECONINCK, Nicolas
dc.contributor.authorKLEIN, Andrea
dc.contributor.authorMASSON, Riccardo
dc.contributor.authorMAZURKIEWICZ-BELDZINSKA, Maria
dc.contributor.authorMERCURI, Eugenio
dc.contributor.authorROSE, Kristy
dc.contributor.authorSERVAIS, Laurent
dc.contributor.authorVLODAVETS, Dmitry
dc.contributor.authorXIONG, Hui
dc.contributor.authorZANOTELI, Edmar
dc.contributor.authorDODMAN, Angela
dc.contributor.authorEL-KHAIRI, Muna
dc.contributor.authorGAKI, Eleni
dc.contributor.authorGERBER, Marianne
dc.contributor.authorGORNI, Ksenija
dc.contributor.authorKLETZL, Heidemarie
dc.contributor.authorBARANELLO, Giovanni
dc.date.accessioned2023-04-04T19:08:53Z
dc.date.available2023-04-04T19:08:53Z
dc.date.issued2022
dc.description.conferencedateAPR 02-07, 2022
dc.description.conferencelocalSeattle, WA
dc.description.conferencenameAnnual Meeting of the American-Academy-of-Neurology
dc.description.indexMEDLINE
dc.description.indexPubMed
dc.description.indexWoS
dc.identifier.citationNEUROLOGY, v.98, n.18, suppl.S, 2022
dc.identifier.eissn1526-632X
dc.identifier.issn0028-3878
dc.identifier.urihttps://observatorio.fm.usp.br/handle/OPI/52637
dc.language.isoeng
dc.publisherLIPPINCOTT WILLIAMS & WILKINSeng
dc.relation.ispartofNeurology
dc.rightsrestrictedAccesseng
dc.rights.holderCopyright LIPPINCOTT WILLIAMS & WILKINSeng
dc.subject.wosClinical Neurologyeng
dc.titleFIREFISH Parts 1 and 2: 24-month Safety and Efficacy of Risdiplam in Type 1 SMAeng
dc.typeconferenceObjecteng
dc.type.categorymeeting abstracteng
dc.type.versionpublishedVersioneng
dspace.entity.typePublication
hcfmusp.affiliation.countryInglaterra
hcfmusp.affiliation.countryChina
hcfmusp.affiliation.countryRússia
hcfmusp.affiliation.countryAustrália
hcfmusp.affiliation.countryPolônia
hcfmusp.affiliation.countryEstados Unidos
hcfmusp.affiliation.countryFrança
hcfmusp.affiliation.countryItália
hcfmusp.affiliation.countrySuíça
hcfmusp.affiliation.countryBélgica
hcfmusp.affiliation.countryisous
hcfmusp.affiliation.countryisofr
hcfmusp.affiliation.countryisobe
hcfmusp.affiliation.countryisoch
hcfmusp.affiliation.countryisoit
hcfmusp.affiliation.countryisopl
hcfmusp.affiliation.countryisoau
hcfmusp.affiliation.countryisoru
hcfmusp.affiliation.countryisocn
hcfmusp.affiliation.countryisogb
hcfmusp.author.externalDARRAS, Basil T.:Harvard Med Sch, Boston Childrens Hosp, Dept Neurol, Boston, MA 02115 USA
hcfmusp.author.externalBOESPFLUG-TANGUY, Odile:Hop Armand Trousseau, I Mot, Paris, France; Univ Paris, NeuroDiderot, UMR 1141, Paris, France
hcfmusp.author.externalDAY, John W.:Stanford Univ, Dept Neurol, Stanford, CA 94305 USA
hcfmusp.author.externalDECONINCK, Nicolas:UZ Gent, Neuromuscular Reference Ctr, Ghent, Belgium; ULB, Ctr Reference Malad Neuromusculaires, Queen Fabiola Childrens Univ Hosp, Brussels, Belgium
hcfmusp.author.externalKLEIN, Andrea:Univ Childrens Hosp Basel, Paediat Neurol, Basel, Switzerland; Univ Bern, Inselspital, Paediat Neurol, Bern, Switzerland
hcfmusp.author.externalMASSON, Riccardo:Fdn IRCCS Ist Neurol Carlo Besta, Dev Neurol Unit, Milan, Italy
hcfmusp.author.externalMAZURKIEWICZ-BELDZINSKA, Maria:Med Univ Gdansk, Dept Dev Neurol, Gdansk, Poland
hcfmusp.author.externalMERCURI, Eugenio:Catholic Univ, Pediat Neurol Inst, Washington, DC USA; Fdn Policlin Gemelli IRCCS, Nemo Pediat, Rome, Italy
hcfmusp.author.externalROSE, Kristy:Childrens Hosp Westmead, Paediat Gait Anal Serv New South Wales, Westmead, NSW, Australia
hcfmusp.author.externalSERVAIS, Laurent:Hop Armand Trousseau, I Mot, Paris, France; MDUK Oxford Neuromuscular Ctr, Dept Paediat, Oxford, England; Univ Hosp Liege, Ctr References Malad Neuromusculaires, Dept Pediat, Div Child Neurol, Liege, Belgium; Univ Liege, Liege, Belgium
hcfmusp.author.externalVLODAVETS, Dmitry:Pirogov Russian Natl Res Med Univ, Russian Children Neuromuscular Ctr, Veltischev Clin Pediat Res Inst, Moscow, Russia
hcfmusp.author.externalXIONG, Hui:Peking Univ First Hosp, Dept Pediat, Beijing, Peoples R China
hcfmusp.author.externalDODMAN, Angela:F Hoffmann La Roche Ltd, Pharma Dev Neurol, Basel, Switzerland
hcfmusp.author.externalEL-KHAIRI, Muna:Roche Prod Ltd, Welwyn Garden City, Herts, England
hcfmusp.author.externalGAKI, Eleni:Roche Prod Ltd, Welwyn Garden City, Herts, England
hcfmusp.author.externalGERBER, Marianne:F Hoffmann La Roche Ltd, Pharma Dev Safety, Basel, Switzerland
hcfmusp.author.externalGORNI, Ksenija:F Hoffmann La Roche Ltd, PDMA Neurosci & Rare Dis, Basel, Switzerland
hcfmusp.author.externalKLETZL, Heidemarie:Roche Innovat Ctr Basel, Roche Pharmaceut Res & Early Dev, Basel, Switzerland
hcfmusp.author.externalBARANELLO, Giovanni:Fdn IRCCS Ist Neurol Carlo Besta, Dev Neurol Unit, Milan, Italy; UCL, NIHR Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England; Great Ormond St Hosp Trust, London, England
hcfmusp.contributor.author-fmusphcEDMAR ZANOTELI
hcfmusp.description.issue18
hcfmusp.description.issuesuppl S
hcfmusp.description.volume98
hcfmusp.origemWOS
hcfmusp.origem.wosWOS:000894020500384
hcfmusp.publisher.cityPHILADELPHIAeng
hcfmusp.publisher.countryUSAeng
relation.isAuthorOfPublication61bd9026-929a-4d06-a8ee-0445b8703e69
relation.isAuthorOfPublication.latestForDiscovery61bd9026-929a-4d06-a8ee-0445b8703e69
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