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https://observatorio.fm.usp.br/handle/OPI/57037
Title: | FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA) |
Authors: | DARRAS, Basil; BARANELLO, Giovanni; BOESPFLUG-TANGUY, Odile; DAY, John; DECONINCK, Nicholas; KLEIN, Andrea; MASSON, Ricardo; MAZURKIEWICZ-BELDZINSKA, Maria; MERCURI, Eugenio; ROSE, Kristy; VLODAVETS, Dmitry; XIONG, Hui; ZANOTELI, Edmar; EL-KHAIRI, Muna; GERBER, Marianne; GORNI, Ksenija; KLETZL, Heidemarie; PALFREEMAN, Laura; DODMAN, Angela; SERVAIS, Laurent |
Citation: | NEUROLOGY, v.100, n.17, suppl.2, article ID 3928, 7p, 2023 |
Appears in Collections: | Comunicações em Eventos - FM/MNE Comunicações em Eventos - HC/ICHC Comunicações em Eventos - LIM/15 Comunicações em Eventos - LIM/45 |
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