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Results 1-10 of 21 (Search time: 0.07 seconds).
Issue Date | Title | Author(s) |
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2021 | IMPACT OF COVID-19 PANDEMIC ON MENTAL HEALTH, SOCIAL CONNECTEDNESS AND COGNITIVE PERFORMANCE OF OLDER ADULTS | SOUZA-TALARICO, Juliana; SILVA, Fernanda; JESUS, Maria Clara; BARBOSA, Breno J. A. P.; NITRINI, Ricardo; BRUCKI, Sonia M. D. |
2021 | FIREFISH Parts 1 and 2: 24-Month Safety and Efficacy of Risdiplam in Type 1 SMA | MASSON, R.; BOESPFLUG-TANGUY, O.; DARRAS, B. T.; DAY, J. W.; DECONINCK, N.; KLEIN, A.; MAZURKIEWICZ-BEDZISKA, M.; MERCURI, E.; ROSE, K.; SERVAIS, L.; VLODAVETS, D.; XIONG, H.; ZANOTELI, E.; DODMAN, A.; EL-KHAIRI, M.; GAKI, E.; GERBER, M.; GORNI, K.; KLETZL, H.; BARANELLO, G. |
2021 | RAINBOWFISH: A study of risdiplam in infants with presymptomatic SMA | BERTINI, E.; AL-MUHAIZEA, M.; FARRAR, M.; NELSON, L.; ARAUJO, A. Prufer de Q. C.; SERVAIS, L.; WANG, Y.; ZANOTELI, E.; EL-KHAIRI, M.; GERBER, M.; GORNI, K.; KLETZL, H.; PALFREEMAN, L.; SCALCO, R. S.; FINKEL, R. |
2021 | Orbicularis Oculi Muscle morphometry alterations in Hemifacial Spasm | GAMEIRO, Gustavo; OSAKI, Midori H.; OSAKI, Teissy; SCHOR, Paulo; MARIE, Suely Kazue Nagahashi; OSAKI, Tammy H. |
2021 | Childhood Amyotrophic Lateral Sclerosis Caused by Excess Sphingolipid Synthesis | MOHASSEL, Payam; DONKERVOORT, Sandra; LONE, Museer A.; NALLS, Matthew A.; GABLE, Kenneth; GUPTA, Sita D.; FOLEY, A. Reghan; HU, Ying; SAUTE, Jonas Alex Morales; MOREIRA, Ana Lucila; KOK, Fernando; INTRONA, Alessandro; LOGROSCINO, Giancarlo; GRUNSEICH, Christopher; NICKOLLS, Alec; POURSHAFIE, Naemeh; NEUHAUS, Sarah B.; SAADE, Dimah; GANGFUSS, Andrea; KOELBEL, Heike; PICCUS, Zoe; PICHON, Claire E. Le; FIORILLO, Chiara; LY, Cindy V.; TOPF, Ana; BRADY, Lauren; SPECHT, Sabine; ZIDELL, Aliza; PEDRO, Helio; MITTELMANN, Eric; THOMAS, Florian P.; CHAO, Katherine R.; KONERSMAN, Chamindra G.; CHO, Megan T.; BRANDT, Tracy; STRAUB, Volker; CONNOLLY, Anne M.; SCHARA, Ulrike; ROOS, Andreas; TARNOPOLSKY, Mark; HOKE, Ahmet; BROWN JR., Robert H.; LEE, Chia-Hsueh; HORNEMANN, Thorsten; DUNN, Teresa M.; BOENNEMANN, Carsten G. |
2021 | IREFISH Parts 1 and 2: 24-month safety and efficacy of risdiplam in type 1 spinal muscular atrophy (SMA) | MASSON, R.; BOESPFLUG-TANGUY, O.; DARRAS, B.; DAY, J.; DECONINCK, N.; KLEIN, A.; MAZURKIEWICZ-BELDZINSKA, M.; MERCURI, E.; ROSE, K.; SERVAIS, L.; VLODAVETS, D.; XIONG, H.; ZANOTELI, E.; DODMAN, A.; EL-KHAIRI, M.; GAKI, E.; GERBER, M.; GORNI, K.; KLETZL, H.; BARANELLO, G. |
2021 | RAINBOWFISH: A study of risdiplam in infants with presymptomatic spinal muscular atrophy (SMA) | SERVAIS, L.; AL-MUHAIZEA, M.; FARRAR, M.; NELSON, L.; PRUFER, A.; FINKEL, R.; WANG, Y.; ZANOTELI, E.; EL-KHAIRI, M.; GERBER, M.; GORNI, K.; KLETZL, H.; PALFREEMAN, L.; SCALCO, R.; BERTINI, E. |
2021 | ANCHOVY: A retrospective cohort study of the natural history of type 1 spinal muscular atrophy (SMA) using medical record data | ZANOTELI, E.; CANCES, C.; VLODAVETS, D.; COMI, G.; MASSON, R.; MAZURKIEWICZ-BELDZINSKA, M.; SAITO, K.; DODMAN, A.; EL-KHAIRI, M.; GORNI, K.; GRAVESTOCK, I.; HOFFART, J.; SCALCO, R.; DARRAS, B. |
2021 | Clinical and genetic spectrum of a large cohort of delta-sarcoglycan muscular dystrophy | ALONSO-PEREZ, J.; GONZALEZ-QUEREDA, L.; BRUNO, C.; PANICUCCI, C.; ALAVI, A.; ZANOTELI, E.; MUELAS, N.; VILCHEZ, J.; DOURADO, E.; KADEM, N.; UMAIR, M.; GUGLIERIR, M.; MARINI-BETTOLO, C.; STRAUB, V.; DIAZ-MANERA, J. |
2021 | Markers of inflammation and neurodegeneration in bipolar disorder older adults | NASCIMENTO, Camila; NUNES, Paula; SUEMOTO, Claudia K.; RODRIGUEZ, Roberta D.; LEITE, Renata E. P.; GRINBERG, Lea; PASQUALUCCI, Carlos Augusto; JACOB-FILHO, Wilson; NITRINI, Ricardo; BRENTANI, Helena Paula; LAFER, Beny |
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