Sistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSPFINKEL, Richard S.FARRAR, Michelle A.VLODAVETS, DmitrySERVAIS, LaurentZANOTELI, EdmarAL-MUHAIZEA, MohammadNELSON, LesliePRUFER, AlexandraWANG, YiFISHER, CarolynGERBER, MarianneGORNI, KsenijaKLETZL, HeidemariePALFREEMAN, LauraSCALCO, RenataBERTINI, Enrico2023-04-042023-04-042022NEUROLOGY, v.98, n.18, suppl.S, 20220028-3878https://observatorio.fm.usp.br/handle/OPI/52633engrestrictedAccessRAINBOWFISH: Preliminary Efficacy and Safety Data in Risdiplam-Treated Infants with Presymptomatic SMAconferenceObjectCopyright LIPPINCOTT WILLIAMS & WILKINSClinical Neurology1526-632X