Sistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSPSERVAIS, L.BARANELLO, G.BOESPFLUG-TANGUY, O.DAY, J.DECONINCK, N.KLEIN, A.MASSON, R.MAZURKIEWICZ-BELDZINSKA, M.MERCURI, E.ROSE, K.VLODAVETS, D.XIONG, H.ZANOTELI, E.EL-KHAIRI, M.GERBER, M.GORNI, K.KLETZL, H.PALFREEMAN, L.DODMAN, A.GAKI, E.DARRAS, B.2023-04-042023-04-042022NEUROMUSCULAR DISORDERS, v.32, suppl.1, p.S88-S88, 20220960-8966https://observatorio.fm.usp.br/handle/OPI/52634engrestrictedAccessFIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy (SMA)conferenceObjectCopyright PERGAMON-ELSEVIER SCIENCE LTD10.1016/j.nmd.2022.07.194Clinical NeurologyNeurosciences1873-2364