Sistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSPDARRAS, Basil T.BOESPFLUG-TANGUY, OdileDAY, John W.DECONINCK, NicolasKLEIN, AndreaMASSON, RiccardoMAZURKIEWICZ-BELDZINSKA, MariaMERCURI, EugenioROSE, KristySERVAIS, LaurentVLODAVETS, DmitryXIONG, HuiZANOTELI, EdmarDODMAN, AngelaEL-KHAIRI, MunaGAKI, EleniGERBER, MarianneGORNI, KsenijaKLETZL, HeidemarieBARANELLO, Giovanni2023-04-042023-04-042022NEUROLOGY, v.98, n.18, suppl.S, 20220028-3878https://observatorio.fm.usp.br/handle/OPI/52637engrestrictedAccessFIREFISH Parts 1 and 2: 24-month Safety and Efficacy of Risdiplam in Type 1 SMAconferenceObjectCopyright LIPPINCOTT WILLIAMS & WILKINSClinical Neurology1526-632X