Sistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSPMIETHKE, Alexander G.PORTA, GildaMOUKARZEL, AdibLIN, Chuan-HaoD'AGOSTINO, DanielMOGUL, Douglas B.NUNES, TiagoAGUILAR, RaulVIG, PamelaCHIOU, Fang KuanTHOMPSON, Richard J.2024-03-082024-03-082023HEPATOLOGY, v.78, suppl.1, p.S2095-S2096, 20230270-9139https://observatorio.fm.usp.br/handle/OPI/58515engrestrictedAccessMARALIXIBAT LEADS TO SIGNIFICANT IMPROVEMENT IN CHOLESTATIC PRURITUS FOR CHILDREN WITH PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS DUE TO TJP2 OR MYO5B DEFICIENCY: DATA FROM THE MARCH-PFIC TRIALconferenceObjectCopyright LIPPINCOTT WILLIAMS & WILKINSGastroenterology & Hepatology1527-3350