FIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophy

Página do item simplificado
dc.contributorSistema FMUSP-HC: Faculdade de Medicina da Universidade de São Paulo (FMUSP) e Hospital das Clínicas da FMUSP
dc.contributor.authorDECONINCK, N.
dc.contributor.authorBARANELLO, G.
dc.contributor.authorBOESPFLUG-TANGUY, O.
dc.contributor.authorDAY, J.
dc.contributor.authorKLEIN, A.
dc.contributor.authorMASSON, R.
dc.contributor.authorMAZURKIEWICZ-BELDZINSKA, M.
dc.contributor.authorMERCURI, E.
dc.contributor.authorROSE, K.
dc.contributor.authorSERVAIS, L.
dc.contributor.authorVLODAVETS, D.
dc.contributor.authorXIONG, H.
dc.contributor.authorZANOTELI, E.
dc.contributor.authorEL-KHAIRI, M.
dc.contributor.authorGERBER, M.
dc.contributor.authorGORNI, K.
dc.contributor.authorKLETZL, H.
dc.contributor.authorDODMAN, A.
dc.contributor.authorGAKI, E.
dc.contributor.authorDARRAS, B.
dc.contributor.groupauthorFIREFISH Working Grp
dc.date.accessioned2022-11-25T13:45:39Z
dc.date.available2022-11-25T13:45:39Z
dc.date.issued2022
dc.description.indexMEDLINEeng
dc.description.sponsorshipF. Hoffmann-La Roche Ltd, Basel, Switzerland
dc.description.sponsorshipF. Hoffmann-La Roche Ltd.
dc.identifier.citationEUROPEAN JOURNAL OF NEUROLOGY, v.29, suppl.1, p.279-279, 2022
dc.identifier.eissn1468-1331
dc.identifier.issn1351-5101
dc.identifier.urihttps://observatorio.fm.usp.br/handle/OPI/50243
dc.language.isoeng
dc.publisherWILEYeng
dc.relation.ispartofEuropean Journal of Neurology
dc.rightsrestrictedAccesseng
dc.rights.holderCopyright WILEYeng
dc.subject.wosClinical Neurologyeng
dc.subject.wosNeuroscienceseng
dc.titleFIREFISH Parts 1 and 2: 36-month safety and efficacy of risdiplam in Type 1 spinal muscular atrophyeng
dc.typeconferenceObjecteng
dc.type.categorymeeting abstracteng
dc.type.versionpublishedVersioneng
dspace.entity.typePublication
hcfmusp.affiliation.countryInglaterra
hcfmusp.affiliation.countryChina
hcfmusp.affiliation.countryBélgica
hcfmusp.affiliation.countryRússia
hcfmusp.affiliation.countryAustrália
hcfmusp.affiliation.countryPolônia
hcfmusp.affiliation.countryItália
hcfmusp.affiliation.countrySuíça
hcfmusp.affiliation.countryEstados Unidos
hcfmusp.affiliation.countryFrança
hcfmusp.affiliation.countryisobe
hcfmusp.affiliation.countryisogb
hcfmusp.affiliation.countryisofr
hcfmusp.affiliation.countryisous
hcfmusp.affiliation.countryisoch
hcfmusp.affiliation.countryisoit
hcfmusp.affiliation.countryisopl
hcfmusp.affiliation.countryisoau
hcfmusp.affiliation.countryisoru
hcfmusp.affiliation.countryisocn
hcfmusp.author.externalDECONINCK, N.:UZ Gent, Neuromuscular Reference Ctr, Ghent, Belgium
hcfmusp.author.externalBARANELLO, G.:UCL, Great Ormond St Hosp Biomed Res Ctr, Great Ormond St Inst Child Hlth, Dubowitz Neuromuscular Ctr NIHR, London, England; Great Ormond St Hosp Trust, London, England
hcfmusp.author.externalBOESPFLUG-TANGUY, O.:I Mot Hop Armand Trousseau, Paris, France
hcfmusp.author.externalDAY, J.:Stanford Univ, Dept Neurol, Palo Alto, CA USA
hcfmusp.author.externalKLEIN, A.:Univ Childrens Hosp Basel, Paediat Neurol, Basel, Switzerland
hcfmusp.author.externalMASSON, R.:Fdn IRCCS Ist Neurol Carlo Besta, Dev Neurol Unit, Milan, Italy
hcfmusp.author.externalMAZURKIEWICZ-BELDZINSKA, M.:Med Univ Gdansk, Dept Dev Neurol, Gdansk, Poland
hcfmusp.author.externalMERCURI, E.:Catholic Univ, Pediat Neurol Inst, Rome, Italy; Fdn Policlin Gemelli IRCCS, Nemo Pediat, Rome, Italy
hcfmusp.author.externalROSE, K.:Univ Sydney, Fac Med & Hlth, Discipline Physiotherapy, Sydney, NSW, Australia; Sydney Childrens Hosp Network, Sydney, NSW, Australia
hcfmusp.author.externalSERVAIS, L.:I Mot Hop Armand Trousseau, Paris, France
hcfmusp.author.externalVLODAVETS, D.:Pirogov Russian Natl Res Med Univ, Russian Children Neuromuscular Ctr, Veltischev Clin Pediat Res Inst, Moscow, Russia
hcfmusp.author.externalXIONG, H.:Peking Univ First Hosp, Dept Pediat, Beijing, Peoples R China
hcfmusp.author.externalEL-KHAIRI, M.:Roche Prod Ltd, Welwyn Garden City, Herts, England
hcfmusp.author.externalGERBER, M.:Pharma Dev Safety F Hoffmann Roche Ltd, Basel, Switzerland
hcfmusp.author.externalGORNI, K.:F Hoffmann Roche Ltd, PDMA Neurosci & Rare Dis, Basel, Switzerland
hcfmusp.author.externalKLETZL, H.:Roche Innovat Ctr Basel, Roche Pharmaceut Res & Early Dev, Basel, Switzerland
hcfmusp.author.externalDODMAN, A.:F Hoffmann Roche Ltd, Pharma Dev Neurol, Basel, Switzerland
hcfmusp.contributor.author-fmusphcEDMAR ZANOTELI
hcfmusp.description.beginpage279
hcfmusp.description.endpage279
hcfmusp.description.issuesuppl 1
hcfmusp.description.volume29
hcfmusp.origemWOS
hcfmusp.origem.wosWOS:000815254001143
hcfmusp.publisher.cityHOBOKENeng
hcfmusp.publisher.countryUSAeng
relation.isAuthorOfPublication61bd9026-929a-4d06-a8ee-0445b8703e69
relation.isAuthorOfPublication.latestForDiscovery61bd9026-929a-4d06-a8ee-0445b8703e69
Arquivos
Coleções
Comunicações em Eventos - FM/MNE
Comunicações em Eventos - HC/ICHC
Comunicações em Eventos - LIM/15